FDA Approved Medical Products for:

Gaucher disease

The table(s) below may not be an exhaustive list of drugs or products used to treat this condition. There may be other products available that are not considered orphan products.

Generic Name Alglucerase injection
Trade Name
(Manufacturer Name)
Ceredase
(Genzyme Corporation)
Indication
The FDA has approved this product to be used in this manner.
Long-term enzyme replacement therapy for children, adolescents and adult patients with a confirmed diagnosis of Type I Gaucher disease who exhibit signs and symptoms that are severe enough to result in one or more of the following conditions: a) moderate-
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Generic Name Imiglucerase
Trade Name
(Manufacturer Name)
Cerezyme®
(Genzyme Corporation)
Indication
The FDA has approved this product to be used in this manner.
Enzyme replacement therapy in patients with type I Gaucher's disease.
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Generic Name Taliglucerase alfa
Trade Name
(Manufacturer Name)
Elelyso For Injection
(Pfizer, Inc.)
Indication
The FDA has approved this product to be used in this manner.
Use as long-term enzyme replacement therapy in patients with Type 1 Gaucher disease
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Generic Name Miglustat
Trade Name
(Manufacturer Name)
Zavesca®
(Actelion Pharmaceuticals Ltd)
Indication
The FDA has approved this product to be used in this manner.
Treatment of mild to moderate Type I Gaucher disease in adults for whom enzyme replacement therapy is not a therapeutic option (e.g., due to constraints such as allergy, hypersensitivity, or poor venous access).
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