FDA Approved Medical Products for:

Glycogen storage disease type 2

The table(s) below may not be an exhaustive list of drugs or products used to treat this condition. There may be other products available that are not considered orphan products.

Generic Name Recombinant human acid alpha-glucosidase
Trade Name
(Manufacturer Name)
(Genzyme Corporation)
The FDA has approved this product to be used in this manner.
For use in patients with Pompe disease (GAA deficiency). Alglucosidase alfa has been shown to improve ventilator-free survival in patients with infantile onset Pompe disease as compared to an untreated historical control, whereas use of Alphaglucosidase
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